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Glycogen Storage Disease - 119 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Extension Study of Long-term Safety and Efficacy of Myozyme in Patients With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored Enzyme Replacement Therapy (ERT) Studies Condición:
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Completed |
Nombre del estudio: Expanded Access Use of Myozyme (Alglucosidase Alfa) in Patients With Late-onset Pompe Disease Condición:
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Approved for marketing |
Nombre del estudio: Expanded Access Use of Myozyme (Alglucosidase Alfa) in Patients With Infantile-onset Pompe Disease Condición:
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Active, not recruiting |
Nombre del estudio: Comparison of the Effect of a Novel Starch (Glycosade) Versus Gastrostomy Tube-Dextrose Infusion on Overnight Euglycaemia Control in Children With Glycogen Storage Disease Type I: Open Label Demonstration Trial Condición:
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Completed |
Nombre del estudio: Newborn Screening Assay of Pompe's Disease Condición: Pompe Disease Fecha: 2008-07-09 Intervenciones: Other: Pompe disease newborn screening DBS will be tested for acid alpha-glucosidase (GAA)activity. Newb |
Terminated |
Nombre del estudio: Study to Evaluate the Safety of AT2220 in Pompe Disease Condición: Pompe Disease Fecha: 2008-05-30 Intervenciones:
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Completed |
Nombre del estudio: Safety and Efficacy of Clenbuterol on Motor Function in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy Condición: Pompe Disease Fecha: 2013-09-11 Intervenciones:
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Recruiting |
Nombre del estudio: A Long Term Follow up Study in Late-onset Pompe Disease Condición: Pompe Disease Fecha: 2008-07-09 |
Recruiting |
Nombre del estudio: A Pilot Study of Pyridostigmine in Pompe Disease Condición: Pompe Disease Fecha: 2015-01-23 Intervenciones: Drug: Pyridostigmine Bromide Pyridostigmine is an acetylcholinesterase inhibitor, which increases the am |